Network
University of Texas Southwestern Medical Center
Organizational unit: University
NE-Lab Pascual
Organizational unit: Division
School of Health Professions
University of Texas Southwestern Medical Center
Organizational unit: School
Neurology & Neurotherapeutics - NE Outside Agreements
Organizational unit: Division
Peter O'Donnell Jr. School of Public Health
Organizational unit: Department
Neurology & Neurotherapeutics - NE Cognitive & Memory Section
Organizational unit: Division
Neurology & Neurotherapeutics - NE Stroke Section
Organizational unit: Division
SPH-Data Sciences in Precision
Peter O'Donnell Jr. School of Public Health
Organizational unit: Division
Office of Clinical Research
Organizational unit: Department
University of Cincinnati
External organization: Academic
University of Texas Southwestern Medical Center
External organization: Academic
National Institute of Neurological Disorders and Stroke
External organization: Unknown
Harvard University
External organization: Academic
Texas Scottish Rite Hospital for Children
External organization: Unknown
Cincinnati Children's Hospital Medical Center
External organization: Medical
University of California at Davis
External organization: Academic
Washington University St. Louis
External organization: Academic
Columbia University
External organization: Academic
University of Utah
External organization: Academic
Unknown
External organization: Unknown
Ohio State University
External organization: Academic
Nationwide Children’s Hospital
External organization: Medical
University of California at Los Angeles
External organization: Academic
Children's National Medical Center
External organization: Medical
Muscular Dystrophy Association
External organization: Unknown
Nemours Children's Clinic
External organization: Unknown
Author National Institutes of Health National Institutes of Health National Institutes of Health
External organization: Unknown
Catholic University of the Sacred Heart
External organization: Academic
University of Pennsylvania
External organization: Academic
National Institutes of Health
External organization: Government
University College London
External organization: Academic
University of Iowa
External organization: Academic
Newcastle University
External organization: Academic
National Center for Research Resources
External organization: Unknown
University of Freiburg
External organization: Academic
Stanford University
External organization: Academic
Sorbonne Université
External organization: Academic
University of Pittsburgh
External organization: Academic
KU Leuven
External organization: Academic
University of Sydney
External organization: Academic
University of Rochester
External organization: Academic
Children's Memorial Hospital
External organization: Medical
Baylor College of Medicine
External organization: Academic
Utrecht University
External organization: Academic
Northwestern University
External organization: Academic
IRCCS Ospedale pediatrico Bambino Gesù - Roma
External organization: Medical
University of Kansas
External organization: Academic
Western University
External organization: Academic
Connecticut Children's Medical Center
External organization: Unknown
Johns Hopkins University
External organization: Academic
Karolinska Institutet
External organization: Academic
University of Colorado Denver
External organization: Academic
Royal Children's Hospital
External organization: Medical
Boston Children's Hospital
External organization: Medical
National Heart Lung and Blood Institute
External organization: Unknown
Spinal Muscular Atrophy Foundation
External organization: Unknown
Oregon Health and Science University
External organization: Academic
St. Jude Children Research Hospital
External organization: Medical
University of Wisconsin-Madison
External organization: Academic
Ionis Pharmaceuticals
External organization: Corporate
University of Florida
External organization: Academic
Biogen IDEC
External organization: Corporate
Biogen
External organization: Unknown
University of Duisburg-Essen
External organization: Academic
University of Colorado Anschutz Medical Campus
External organization: Academic
Sydney Children's Hospital
External organization: Medical
Children's Medical Center Dallas
External organization: Unknown
University of Minnesota Twin Cities
External organization: Academic
Hammersmith Hospital
External organization: Medical
PTC Therapeutics
External organization: Unknown
Medical Research Foundation and Medical Research Council
External organization: Unknown
University of Helsinki
External organization: Academic
University of Lausanne
External organization: Academic
University of Massachusetts Medical School
External organization: Academic
Centro Clinico Nemo
External organization: Unknown
National Human Genome Research Institute
External organization: Unknown
PTC Therapeutics
External organization: Corporate
Vanderbilt University
External organization: Academic
University of Gothenburg
External organization: Academic
Queen Elizabeth II Medical Centre Trust
External organization: Unknown
University of Tennessee Health Science Center
External organization: Academic
University of Western Australia
External organization: Academic
Association Française contre les Myopathies
External organization: Unknown
Duke University
External organization: Academic
Rush University
External organization: Academic
SUNY Upstate Medical University
External organization: Academic
Tokyo Women's Medical University
External organization: Academic
Broad Institute
External organization: Academic
Massachusetts General Hospital
External organization: Medical
Hospital Universitario La Fe
External organization: Medical
National Institutes of Health, Bethesda
External organization: Unknown
Roche
External organization: Unknown
Institut national de la santé et de la recherche médicale
External organization: Government
Onze Lieve Vrouwe Gasthuis
External organization: Medical
University of Padua
External organization: Academic
Children's Hospital and Regional Medical Center Seattle
External organization: Medical
University of Arizona
External organization: Academic
Hôpital de la Timone
External organization: Unknown
University of Miami
External organization: Academic
Wellcome Trust
External organization: Academic
IRCCS Istituto Eugenio Medea - Bosisio Parini (LC)
External organization: Medical
University of Michigan, Ann Arbor
External organization: Academic
University of Melbourne
External organization: Academic
Dorenbecher Children's Hospital
External organization: Unknown
Novartis Gene Therapies
External organization: Unknown
Mayo Clinic Rochester, MN
External organization: Medical
University of Campania Luigi Vanvitelli
External organization: Academic
SMA Foundation
External organization: Unknown
University of Texas at Austin
External organization: Academic
VA Medical Center
External organization: Medical
The Children's Hospital of Philadelphia
External organization: Medical
Great Ormond Street Hospital for Children Foundation Trust
External organization: Unknown
Virginia Commonwealth University
External organization: Academic
Universite de Lille 2
External organization: Academic
University of Milan
External organization: Academic
Harvard Center for Mendelian Genomics
External organization: Unknown
University of New South Wales
External organization: Academic
University of Calgary
External organization: Academic
Sarepta Therapeutics
External organization: Corporate
Santhera Pharmaceuticals
External organization: Unknown
Leiden University
External organization: Academic
Luminesce Alliance
External organization: Unknown
University of California at San Diego
External organization: Academic
European Neuromuscular Centre
External organization: Unknown
University of Barcelona
External organization: Academic
University of Toronto
External organization: Academic
George Washington University
External organization: Academic
NHS Foundation Trust
External organization: Unknown
University of Cologne
External organization: Academic
4Pharma
External organization: Unknown
Rady Children's Hospital
External organization: Medical
Royal Perth Hospital
External organization: Medical
Shriners Hospitals for Children
External organization: Medical
Emory University
External organization: Academic
National Center for Advancing Translational Sciences
External organization: Unknown
Hacettepe University
External organization: Academic
Novartis Gene Therapies, Inc.
External organization: Unknown
University of Central Florida
External organization: Academic
Deutsche Gesellschaft für Muskelkranke
External organization: Unknown
Santhera Pharmaceuticals
External organization: Unknown
March of Dimes Foundation
External organization: Unknown
Novartis USA
External organization: Corporate
University of Liege
External organization: Academic
University of Louisville
External organization: Academic
University of Texas Health Science Center at San Antonio
External organization: Academic
California Pacific Medical Center
External organization: Medical
Novartis
External organization: Unknown
Fondazione Telethon
External organization: Unknown
Ann and Robert H. Lurie Children's Hospital of Chicago
External organization: Unknown
Cure SMA
External organization: Unknown
Medical College of Wisconsin
External organization: Academic
AveXis/Novartis
External organization: Unknown
IRCCS Istituto Ortopedico Rizzoli - Bologna
External organization: Medical
Medical University of Warsaw
External organization: Academic
Division of Research Resources
External organization: Unknown
McGill University
External organization: Academic
The Children's Hospital at Westmead
External organization: Medical
Social Trends Institute
External organization: Unknown
Spectrum Health
External organization: Medical
Pfizer
External organization: Corporate
MetroHealth Medical Center Cleveland
External organization: Medical
University of Illinois at Chicago
External organization: Academic
Astrid Lindgren Children Hospital
External organization: Unknown
Australian National Health and Medical Research Council
External organization: Unknown
Hôpital Raymond Poincaré
External organization: Medical
Inc.
External organization: Unknown
Children's Hospital
External organization: Unknown
University of Connecticut
External organization: Academic
King's College London
External organization: Academic
Edgewise Therapeutics and Sarepta Therapeutics
External organization: Unknown
Murdoch Children's Research Institute
External organization: Academic
New South Wales Government
External organization: Unknown
Children's Health
External organization: Unknown
Clinic for Special Children
External organization: Unknown
University of Copenhagen
External organization: Academic
University of Amsterdam
External organization: Academic
Texas A&M University
External organization: Academic
University of Groningen
External organization: Academic
Shifa International Hospital
External organization: Unknown
Parent Project Muscular Dystrophy
External organization: Unknown
PharmOptima
External organization: Unknown
University of Mississippi
External organization: Academic
Lancaster General Hospital
External organization: Medical
Children’s Medical Research Institute
External organization: Unknown
Medical University of South Carolina
External organization: Academic
University of Virginia
External organization: Academic
University of Washington
External organization: Academic
Rutgers - The State University of New Jersey, Newark
External organization: Academic
Universite Claude Bernard Lyon 1
External organization: Academic
Tel Aviv University
External organization: Academic
Ohio State Wexner Medical Center
External organization: Unknown
Child Neurology Center of Northwest Florida
External organization: Unknown
Radboud University Nijmegen
External organization: Academic
Rehabiliterings Center for Muskelsvind
External organization: Unknown
U.S. Public Health Service
External organization: Unknown
University of Valencia
External organization: Academic
Imperial College London
External organization: Academic
G.v. Preyer'sches Kinderspital
External organization: Unknown
University of Oxford
External organization: Academic
National Institute for Child Health and Human Development
External organization: Unknown
Newcastle upon Tyne Hospitals NHS Foundation Trust
External organization: Medical
FibroGen
External organization: Unknown
Queen Fabiola Children's University Hospital
External organization: Medical
Sarepta Therapeutics
External organization: Unknown
Hennepin County Medical Center
External organization: Medical
SMA Europe
External organization: Unknown
Royal Manchester Children's Hospital
External organization: Medical
Broadstreet HEOR
External organization: Unknown
Ionis Pharmaceuticals
External organization: Unknown
Cornell University
External organization: Academic
Pittsburgh Liver Research Center, University of Pittsburgh
External organization: Unknown
University of Florence
External organization: Academic
Harvard University, University of Chicago
External organization: Unknown
National Jewish Health and University of Colorado
External organization: Unknown
Vasa Central Hospital
External organization: Unknown
Université de Strasbourg
External organization: Academic
Center for Mendelian Genomics, University of Washington
External organization: Unknown
Hôpital-Femme-Mère-Enfant
External organization: Unknown
Folkhalsan
External organization: Unknown
Hospital for Special Care New Britain
External organization: Unknown
Muskelsvindfonden
External organization: Unknown
AveXis/Novartis Gene Therapies
External organization: Unknown
Swiss Federal Institute of Technology Lausanne
External organization: Academic
Université Paris 5
External organization: Academic
Henry Ford Health System
External organization: Medical
Gillette Children's Specialty Healthcare
External organization: Medical
Sahlgrenska University Hospital
External organization: Medical
Kay Square Scientific
External organization: Unknown
NIHR Biomedical Research Center for Aging
External organization: Unknown
Clinical Data Science GmbH
External organization: Unknown
Basque Coast Hospital Center
External organization: Unknown
Rhone-Poulenc Rorer
External organization: Unknown
Great Ormond Street Children's Hospital for the Dubowitz Neuromuscular Center
External organization: Unknown
Children's Hospital of Philadelphia
External organization: Unknown
Newton Fund
External organization: Unknown
Universidade de São Paulo
External organization: Academic
University of South Florida
External organization: Academic
Spica Consultants Ltd
External organization: Unknown
Deutsche Forschungsgemeinschaft
External organization: Unknown
University of South Carolina
External organization: Academic
Pontificia Universidad Católica de Chile
External organization: Academic
Université de Bretagne Occidentale
External organization: Academic
Université catholique de Louvain
External organization: Academic
Foye family
External organization: Unknown
Department of Neurology
External organization: Unknown
Audentes Therapeutics
External organization: Unknown
The University of Chicago
External organization: Academic
Paediatric Neuroservices
External organization: Unknown
French Muscular Dystrophy Association
External organization: Unknown
Verein zur Erforschung von Muskelkrankheiten bei Kindern
External organization: Unknown
National Institute for Health and Care Research
External organization: Unknown
The University of Sydney
External organization: Unknown
University of Exeter
External organization: Academic
University of Arkansas for Medical Sciences
External organization: Unknown
Office of Rare Diseases Research
External organization: Unknown
University of Puerto Rico
External organization: Academic
National Institutes of Health
External organization: Unknown
Pennsylvania State University Hershey
External organization: Academic
Tufts Medical Center
External organization: Medical
Dept. of Nutrition-WG 48
External organization: Unknown
The Pediatric Neuromuscular Clinical Research Network
External organization: Unknown
Norton's Children's Hospital
External organization: Unknown
Cancer Prevention and Research Institute of Texas
External organization: Unknown
Aga Khan University
External organization: Academic
Lawrence Livermore National Laboratory
External organization: Government
NIHR Royal Brompton Cardiovascular Biomedical Research Unit
External organization: Unknown
Agence Nationale de la Recherche NADKiller
External organization: Unknown
Slaney Family Fund
External organization: Unknown
Department of Physical Therapy
External organization: Unknown
Carleton University
External organization: Academic
Harvard Medical School Landry
External organization: Unknown
Royal Victoria Hospital Belfast
External organization: Medical
Centers for Disease Control and Prevention
External organization: Unknown
Shire
External organization: Unknown
F. Hoffmann-La Roche AG
External organization: Corporate
Shriner's Hospital Research Fund
External organization: Unknown
NIH Wellstone Muscular Dystrophy Center
External organization: Unknown
Université libre de Bruxelles
External organization: Academic
Minnesota Department of Agriculture
External organization: Government
Duchenne Research Fund
External organization: Unknown
Nagoya University
External organization: Academic
Seattle Children's Hospital
External organization: Unknown
Vereniging Spierziekten Nederland
External organization: Unknown
Woman-Mother-Child Hospital (HFME)
External organization: Unknown
Rehabilitation and Regenerative Medicine
External organization: Unknown
NIH Clinical Center
External organization: Unknown
Massachusetts Institute of Technology
External organization: Academic
University of Southern California
External organization: Academic
Genentech-Roche
External organization: Unknown
Institut de Myologie
External organization: Unknown
NINDS CDE Project and NLM CDE
External organization: Unknown
Department of Physical Therapy
External organization: Unknown
Swedish Medical Center
External organization: Medical
Nemours
External organization: Unknown
Schweizerischer Nationalfonds zur Förderung der Wissenschaftlichen Forschung
External organization: Unknown
Hadassah University Medical Centre
External organization: Medical
Canadian Institutes of Health Research
External organization: Government
Swedish Cancer Foundation
External organization: Unknown
Autonomous University of Barcelona
External organization: Academic
IRCCS Istituto Giannina Gaslini - Genova
External organization: Medical
Otonomy
External organization: Unknown
University of British Columbia
External organization: Academic
McGill University
External organization: Unknown
University of Ottawa
External organization: Academic
McMaster University
External organization: Academic
Biologics Consulting Group Inc.
External organization: Unknown
City, University of London
External organization: Academic
Departments of Neurology
External organization: Unknown
Prinses Beatrix Spierfonds
External organization: Unknown
University of Tübingen
External organization: Academic
SUNY Downstate Health Sciences University
External organization: Academic
University of Turin
External organization: Academic
Taysha Gene Therapies
External organization: Unknown
Children's Medical Center Dallas
External organization: Medical
NIH/NCATS
External organization: Unknown
CHU de Nancy
External organization: Medical
European Union’s Horizon 2020 European Research Council
External organization: Unknown
Scripps Research Institute
External organization: Unknown
Westmead Hospital
External organization: Medical
Muscular Dystrophy Association of Finland
External organization: Unknown
Children’s Cancer Institute
External organization: Unknown
Women's and Children's Hospital Adelaide
External organization: Medical
Division of Neurology
External organization: Unknown
Hospital Dr. Luis Calvo Mackenna Hospital
External organization: Unknown
National Institute for Health Research Health Protection Research Unit
External organization: Unknown
Seoul National University
External organization: Academic
US Government
External organization: Unknown
Motol University Hospital
External organization: Medical
Howard Hughes Medical Institute
External organization: Academic
Freiberg University of Mining and Technology
External organization: Academic
Children’s Hospital of Philadelphia
External organization: Unknown
Cure Congenital Muscular Dystrophy (Cure CMD)
External organization: Unknown
Critical Path Institute
External organization: Unknown
CHU de Nantes
External organization: Medical
KU
External organization: Unknown
Shriner's Hospital
External organization: Unknown
KRLD CBS News Radio 1080
External organization: Unknown
Medicinska Understödsföreningen Liv och Hälsa
External organization: Unknown
National Research Center
External organization: Government
Princes Beatrix Fonds
External organization: Unknown
Danish National Rehabilitation Center for Neuromuscular Diseases
External organization: Unknown
Université d'Angers
External organization: Academic
PharmaGenesis London
External organization: Unknown
University College London Hospitals NHS Foundation Trust
External organization: Unknown
Peninsula Medical School Universities of Exeter and Plymouth
External organization: Academic
University of Bonn
External organization: Academic
Stiftung für die Erforschung der Muskelkrankheiten
External organization: Unknown
Bielefeld University
External organization: Academic
Project Cure
External organization: Unknown
Yale University
External organization: Academic
Rhode Island Hospital
External organization: Unknown
Broad Institute of MIT
External organization: Unknown
University of Würzburg
External organization: Academic
Muscular Dystrophy Campaign
External organization: Unknown
Children's Hospital Philadelphia
External organization: Unknown
Ministero della Salute
External organization: Government
Friedrich-Alexander University Erlangen-Nürnberg
External organization: Academic
National Institute of Dental and Craniofacial Research
External organization: Unknown
Goryeb Children's Hospital
External organization: Unknown
Sarepta Therapeutics
External organization: Unknown
Netherlands Organization for Health Research and Development
External organization: Unknown
Pfizer
External organization: Unknown
Alberta Children's Hospital
External organization: Medical
University of Cambridge
External organization: Academic
GENOPOLE
External organization: Academic
University of Texas Health Science Center at Houston
External organization: Academic
SUNY Buffalo
External organization: Academic
TRiNDS
External organization: Unknown
Cambridge University Hospitals NHS Foundation Trust
External organization: Medical
Central Texas Neurosurgery for Children
External organization: Unknown
Department of Advanced Practice, Children's Medical Center of Dallas
External organization: Unknown
NIH CDE
External organization: Unknown
Kaiser Permanente
External organization: Medical
Netherlands ALS Foundation
External organization: Unknown
Data and Safety Monitoring Committee
External organization: Unknown
Neuromuscular Foundation of Western Australia
External organization: Unknown
National Institute of Arthritis and Musculoskeletal and Skin Diseases
External organization: Unknown
Institute of Genetic Medicine
External organization: Unknown
University of Arkansas for Medical Sciences
External organization: Academic
Humboldt University of Berlin
External organization: Academic
University of California at San Francisco
External organization: Academic
Brigham and Women’s Hospital
External organization: Medical
Myriad RBM
External organization: Unknown
PathWest Laboratory Medicine WA
External organization: Academic
Universite Paris Saclay
External organization: Academic
Guy's Hospital
External organization: Medical
Children’s Cancer Institute
External organization: Unknown
Royal College of Physicians
External organization: Academic
University of New Mexico
External organization: Academic
Seventh Framework Programme
External organization: Unknown
Tampere University
External organization: Academic
Human Genetics Unit
External organization: Unknown
Hyundai Hope on Wheels Foundation
External organization: Unknown
SLC6A1 Connect
External organization: Unknown
National Institute of Diabetes and Digestive and Kidney Diseases
External organization: Unknown
Lily Foundation
External organization: Unknown
Boston College
External organization: Academic
Royal Australasian College of Physicians
External organization: Unknown
Ottawa Hospital Research Institute
External organization: Unknown
Mitochondrial Disease Patient Cohort
External organization: Unknown
University of Utah
External organization: Unknown
Guy's and St Thomas' NHS Foundation Trust
External organization: Medical
Concord Repatriation General Hospital
External organization: Medical
Stony Brook University
External organization: Academic
Case Western Reserve University
External organization: Academic
Northwest Florida Clinical Research Group
External organization: Unknown
Stichting Spieren voor Spieren
External organization: Unknown
US Public Health Service National Research Service
External organization: Unknown
John Hunter Children's Hospital
External organization: Unknown
University of Leicester
External organization: Academic
UK/Turkey
External organization: Unknown
Pharmacopeia Incorporated, Cranbury
External organization: Unknown
The Robert Jones and Agnes Hunt Orthopaedic and District Hospital NHS Trust
External organization: Medical
Texas Children's Hospital Houston
External organization: Medical
Cedars-Sinai Medical Center
External organization: Medical
UK NHS
External organization: Unknown
Royal Children's Hospital
External organization: Unknown
Optum Global Solutions
External organization: Unknown
Children's Cancer Research Fund
External organization: Unknown
Fondation Leducq
External organization: Unknown
Institut de Myologie
External organization: Unknown
BG Medicine
External organization: Unknown
Akron Children's Hospital
External organization: Unknown
Alfred Health
External organization: Medical
Demter/Ichorion Therapeutics
External organization: Unknown
MRC Centre for Neuromuscular Diseases
External organization: Unknown
BD Diagnostics
External organization: Unknown
Clinical Genetic Service
External organization: Unknown
SMA Foundation and Working on Walking Fund
External organization: Unknown
Department of Veterans Affairs
External organization: Government
Monash University
External organization: Academic
Kinsman Foundation
External organization: Unknown
Université Paris 7
External organization: Academic
Invitae Corp.
External organization: Unknown
Nashoba Valley Healthcare Group
External organization: Unknown
Mercy Clinic
External organization: Unknown
Sarepta Ther apeutics, Inc.
External organization: Unknown
Huggenberger Foundation and Swiss National Science Foundation
External organization: Unknown
Orthocare Innovations
External organization: Corporate
Coriell Institute for Medical Research
External organization: Unknown
Cytokinetics
External organization: Unknown
Children's Home Society of Virginia
External organization: Unknown
Prevention Genetics
External organization: Unknown
Optum Lifesciences Wolfeboro
External organization: Unknown
University of Texas Rio Grande Valley
External organization: Academic
Johannes Gutenberg University Mainz
External organization: Academic
Brown University
External organization: Academic
Departments of Neurology and Pediatrics
External organization: Unknown
Ludwig Maximilian University of Munich
External organization: Academic
Svenska Kulturfonden
External organization: Unknown
Connecticut Medical Center
External organization: Unknown
California Department of Education
External organization: Unknown
OPKO Health, Inc.
External organization: Corporate
E-Rare project GENOMIT
External organization: Unknown
Université Paris Cité
External organization: Academic
Excel Scientific Solutions
External organization: Unknown
Hasbro Children's Hospital
External organization: Medical
G. v. Preyer'sches Kinderspital
External organization: Unknown
British Columbia Hospital
External organization: Unknown
Children's Hospital Medical Center
External organization: Unknown
Government of Western Australia Department of Health FutureHealth WA
External organization: Unknown
University of Denver
External organization: Academic
Childreńs Medical Center Dallas
External organization: Unknown
Juselius Foundation
External organization: Unknown
Academy of Finland
External organization: Academic
Service de Génétique Médicale
External organization: Unknown
Maine Medical Center
External organization: Medical
Dubowitz Neuromuscular Centre
External organization: Unknown
U.S. Food and Drug Administration
External organization: Unknown
King's College Hospital
External organization: Medical
St. Joseph's Hospital and Medical Center, Phoenix
External organization: Medical
St. Louis Children’s Hospital
External organization: Unknown
Resource Centre for Oral Health in Rare Medical Conditions
External organization: Unknown
Walker Bioscience
External organization: Unknown
Royal Devon & Exeter NHS Foundation Trust
External organization: Medical
Scottish Microbiology Association
External organization: Unknown
Thomas Jefferson University
External organization: Academic
University of Manchester
External organization: Academic
Carolinas Medical Center
External organization: Medical
Universidad Autónoma de Madrid
External organization: Academic
Driscoll Children's Hospital
External organization: Unknown
Istanbul University
External organization: Academic
Cidade Universitária–Ilha do Fundão
External organization: Unknown
Universidad Nacional Autónoma de México
External organization: Academic
U.S. Department of Defense
External organization: Unknown
Centre Hospitalier, France
External organization: Medical
New England Research Institutes
External organization: Corporate
American Academy of Neurology
External organization: Unknown
Polclinico Gemell, Largo Gemelli
External organization: Unknown
Medical College of Georgia
External organization: Academic
Children's Hospital
External organization: Unknown
International Center for Genomic Medicine in Neuromuscular Disease
External organization: Unknown
Addenbrooke's Hospital
External organization: Medical
Montefiore Health System
External organization: Medical
EU Joint Programme – Neurodegenerative Disease Research
External organization: Unknown
BioMarin Pharmaceutical Inc.
External organization: Corporate
Aix Marseille Universite
External organization: Academic
University of Texas at Dallas
External organization: Academic
European Commission
External organization: Academic
Institute of Motion
External organization: Unknown
Murdoch University
External organization: Academic
University of Texas Southwestern
External organization: Unknown
Andrew McDonough B+ Foundation
External organization: Unknown
COMBINEDBrain
External organization: Unknown
Samantha Baxter
External organization: Unknown
Hôpital Saint Vincent de Paul
External organization: Medical
CNRS Centre National de la Recherche Scientifique
External organization: Academic
Andrew's Buddies
External organization: Unknown
The EMMES Corporation
External organization: Unknown
Cure CMD
External organization: Unknown
Broadstreet Health Economics Outcomes Research
External organization: Unknown
Amsterdam UMC
External organization: Unknown
Genentech Incorporated
External organization: Corporate
Pathology Society
External organization: Unknown
University of Alabama at Birmingham
External organization: Academic
Institute of Myology
External organization: Unknown
University College London
External organization: Unknown
Alfaisal University
External organization: Academic
Cook Children's Medical Center
External organization: Unknown
Childrens Healthcare of Atlanta
External organization: Unknown
Newcastle Upon Tyne Hospitals NHS Foundation Trust
External organization: Unknown
Blue Cross and Blue Shield Association
External organization: Corporate
Indiana University Bloomington
External organization: Academic
University Hospital Southampton NHS Foundation Trust
External organization: Medical
Royal Prince Alfred Hospital
External organization: Medical
NINDS/NIH
External organization: Unknown
Finska Läkaresällskapet
External organization: Unknown
Athena Diagnostics, Inc.
External organization: Unknown