A consolidated AAV system for single-cut CRISPR correction of a common Duchenne muscular dystrophy mutation

Yu Zhang, Takahiko Nishiyama, Hui Li, Jian Huang, Ayhan Atmanli, Efrain Sanchez-Ortiz, Zhaoning Wang, Alex A. Mireault, Pradeep P.A. Mammen, Rhonda Bassel-Duby, Eric N. Olson

Research output: Contribution to journalArticlepeer-review

18 Scopus citations

Fingerprint

Dive into the research topics of 'A consolidated AAV system for single-cut CRISPR correction of a common Duchenne muscular dystrophy mutation'. Together they form a unique fingerprint.

Medicine & Life Sciences