Intrathecal enzyme replacement therapy reverses cognitive decline in mucopolysaccharidosis type I

Igor Nestrasil, Elsa Shapiro, Alena Svatkova, Patricia Dickson, Agnes Chen, Amy Wakumoto, Alia Ahmed, Edward Stehel, Sarah McNeil, Curtis Gravance, Elizabeth Maher

Research output: Contribution to journalArticlepeer-review

25 Scopus citations

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Medicine & Life Sciences