Novel Cross-Correction–Enabled Gene Therapy for CDKL5-Deficiency Disorder

Felix Nitschke, Alina Peraza Montalbano

Research output: Contribution to journalComment/debatepeer-review

Original languageEnglish (US)
JournalNeurotherapeutics
DOIs
StateAccepted/In press - 2022

Keywords

  • AAVPHP
  • CDKL5 deficiency
  • Cross-correction
  • Enzyme replacement therapy
  • Gene replacement therapy
  • TAT

ASJC Scopus subject areas

  • Pharmacology
  • Clinical Neurology
  • Pharmacology (medical)

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