Nusinersen, an antisense oligonucleotide drug for spinal muscular atrophy

Research output: Contribution to journalArticle

85 Scopus citations
Original languageEnglish (US)
JournalNature Neuroscience
DOIs
StateAccepted/In press - Feb 13 2017

ASJC Scopus subject areas

  • Neuroscience(all)

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