Nusinersen in later-onset spinal muscular atrophy: Long-term results from the phase 1/2 studies

Basil T. Darras, Claudia A. Chiriboga, Susan T. Iannaccone, Kathryn J. Swoboda, Jacqueline Montes, Laurence Mignon, Shuting Xia, C. Frank Bennett, Kathie M. Bishop, Jeremy M. Shefner, Allison M. Green, Peng Sun, Ishir Bhan, Sarah Gheuens, Eugene Schneider, Wildon Farwell, Darryl C. De Vivo

Research output: Contribution to journalArticlepeer-review

182 Scopus citations

Fingerprint

Dive into the research topics of 'Nusinersen in later-onset spinal muscular atrophy: Long-term results from the phase 1/2 studies'. Together they form a unique fingerprint.

Medicine & Life Sciences