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Dive into the research topics of 'Phase 1 gene therapy for duchenne muscular dystrophy using a translational optimized AAV vector'. Together they form a unique fingerprint.- Sort by
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Dawn E. Bowles, Scott W.J. McPhee, Chengwen Li, Steven J. Gray, Jade J. Samulski, Angelique S. Camp, Juan Li, Bing Wang, Paul E. Monahan, Joseph E. Rabinowitz, Joshua C. Grieger, Lakshmanan Govindasamy, Mavis Agbandje-Mckenna, Xiao Xiao, R. Jude Samulski
Research output: Contribution to journal › Article › peer-review