Precise in vivo genome editing via single homology arm donor mediated intron-targeting gene integration for genetic disease correction

Keiichiro Suzuki, Mako Yamamoto, Reyna Hernandez-Benitez, Zhe Li, Christopher Wei, Rupa Devi Soligalla, Emi Aizawa, Fumiyuki Hatanaka, Masakazu Kurita, Pradeep Reddy, Alejandro Ocampo, Tomoaki Hishida, Masahiro Sakurai, Amy N. Nemeth, Estrella Nuñez Delicado, Josep M. Campistol, Pierre Magistretti, Pedro Guillen, Concepcion Rodriguez Esteban, Jianhui GongYilin Yuan, Ying Gu, Guang Hui Liu, Carlos López-Otín, Jun Wu, Kun Zhang, Juan Carlos Izpisua Belmonte

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Medicine & Life Sciences