Nusinersen versus sham control in later-onset spinal muscular atrophy

E. Mercuri, B. T. Darras, C. A. Chiriboga, J. W. Day, C. Campbell, A. M. Connolly, S. T. Iannaccone, J. Kirschner, N. L. Kuntz, K. Saito, P. B. Shieh, M. Tulinius, E. S. Mazzone, J. Montes, K. M. Bishop, Q. Yang, R. Foster, S. Gheuens, C. F. Bennett, W. FarwellE. Schneider, D. C. De Vivo, R. S. Finkel

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